FDA Finally Approves First Ever Treatment Drug – Finally!

100 days after the FDA’s legally mandated decision date,the FDA announced accelerated approval for  Eteplirsen by Sarepta Therapeutics.  Eteplirsen is the first therapy drug approved for Duchenne which works to skip over the deleted exons.  The approval did come without bureaucratic “drama” and in-fighting.  There were definite opponents for approval, based on the nonsense of […]